Amryt Pharmaceuticals Designated Activity Company
- Address
- 45 Mespil Road, Ballsbridge
Sponsor Overview
Specializations
Generalised Lipodystrophy
Clinical development activity is centered on generalised lipodystrophy, with a focus on the metabolic and endocrine complications associated with this rare disease.
- Metabolic disease
- Diabetes mellitus
- Hypertriglyceridaemia
Research interest extends to the management of severe adipose tissue disorders in very young children, reflecting attention to early-life rare disease care.
Paediatric Rare Disease Care
The sponsor’s research landscape includes paediatric treatment needs in children under 6 years of age, addressing a highly specialised population within rare diseases.
- Early childhood intervention
- Childhood metabolic complications
- Rare paediatric endocrinology
This area reflects a therapeutic emphasis on conditions where growth, metabolic regulation, and long-term disease burden are closely linked.
Endocrine and Lipid Disorders
Trials funded by the sponsor also align with the treatment of endocrine disorders and severe lipid abnormalities, particularly where these overlap with inherited metabolic disease.
- Lipid metabolism
- Insulin resistance
- Triglyceride elevation
The therapeutic focus includes clinical problems arising from defective adipokine signaling and related systemic metabolic imbalance.
Sponsored Trials
| Trial Name | Country | Status |
|---|---|---|
| Open-label, Phase 3b study to evaluate effectiveness, safety and pharmacokinetic parameters of metreleptin in patients under 6 years of age with generalised lipodystrophy and associated diabetes mellitus and/or hypertriglyceridaemia |  Belgium France Germany Italy | Not Recruiting |
Data & Insights
This sponsor works with 1 molecule, of which 0 are not being studied by other sponsors.
This sponsor has worked with 12 sites across their trial portfolio.
Therapeutic Focus
- 1.Metabolism1 trial38 other sponsors
Partnered Research Centres
12 centres- Address
- Via Sergio Pansini 5, 80131 Naples
- Address
- Viale Antonio Gramsci 14, 43126 Parma
- Address
- Corso Giuseppe Mazzini 18, 28100 Novara
- Address
- Via Dei Vestini Snc, 66100 Chieti
- Address
- Viale Luigi Borri N 57, 21100 Varese
- Address
- 149 Rue De Sevres, 75015 Paris
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