Yoann H.
- Country
- France
- Department
- Site Hôpital des Enfants, Competence and Resources Center for Constitutional Hemorrhagic Disorders
Research Overview
- A phase 3b open-label, multicenter study evaluating physical activity and joint health in previously treated patients ≥12 years of age with severe haemophilia A treated with intravenous recombinant coagulation factor VIII Fc-von Willebrand Factor-XTEN fusion protein (rFVIIIFc-VWF-XTEN; efanesoctocog alfa) for 24 months
- Efficacy and Safety Evaluation of Mitapivat in Pediatric Patients with Pyruvate Kinase Deficiency Not Receiving Regular Transfusions: A Phase 3, Multicenter, Randomized, Double-blind, Placebo-Controlled Study
- Continuation Study on Efanesoctocog Alfa for Safety and Efficacy in Severe Haemophilia A Patients Post-Previous Trial Completion
Data & Insights
Has run more than one trial at 13 of 50 partner sites.
Specializations
Hematological Disorders
The investigator specializes in treating various blood disorders, with particular emphasis on hemophilia A and von Willebrand Disease. Their research focuses on innovative therapeutic approaches for managing these conditions.
- Severe Hemophilia A Management
- Pediatric Von Willebrand Disease Treatment
- Bleeding Episode Control
Their work extends to both prophylactic treatments and acute bleeding management strategies.
Pediatric Hematology
The investigator demonstrates particular expertise in treating blood disorders in children, focusing on hereditary blood conditions and their specific manifestations in pediatric populations.
- Pediatric Blood Disorder Management
- Hereditary Disease Treatment
- Long-term Patient Care
Their research encompasses comprehensive treatment approaches for young patients with various blood disorders.
Metabolic Blood Disorders
The investigator has developed expertise in treating Pyruvate Kinase Deficiency, focusing on innovative therapeutic approaches for patients who are not dependent on regular blood transfusions.
- Hemoglobin Management
- Non-transfusion Dependent Therapy
- Long-term Treatment Strategies
Their work includes evaluating novel treatments for rare metabolic blood disorders.
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