Stephanie D.
- Country
- Belgium
- Department
- Neurology
Research Overview
- A Phase 2 Randomized, Double-blind, Placebo-controlled Study to Evaluate the Effect of EDG-5506 on Safety, Biomarkers, Pharmacokinetics, and Functional Measures in Adults and Adolescents with Becker Muscular Dystrophy
- Long-term Safety, Tolerability, and Efficacy of Subcutaneous Efgartigimod PH20 in Chronic Inflammatory Demyelinating Polyneuropathy: An Open-label Extension Study
- Long-term Safety and Biomarker Assessment of EDG-5506 in Adults and Adolescents with Becker Muscular Dystrophy: An Open-Label Extension Study
Data & Insights
Has run more than one trial at 72 of 169 partner sites.
Specializations
Neuromuscular Disorders
This investigator specializes in treating various forms of muscular dystrophy and neuromuscular conditions, with particular focus on Becker Muscular Dystrophy (BMD) and Type 3 Spinal Muscular Atrophy. Their research explores therapeutic interventions for muscle strength preservation and function improvement.
- Muscle Strength Assessment
- Creatine Kinase Monitoring
- Pediatric and Adult Treatment Approaches
The investigator's work encompasses both adult and adolescent patient populations, focusing on innovative therapeutic solutions.
Neurological Disorders
Primary research interests include Amyotrophic Lateral Sclerosis (ALS) and Charcot-Marie-Tooth Disease. The investigator studies interventions aimed at managing disease progression and improving patient outcomes.
- Ventilation-Free Survival Assessment
- Functional Capacity Evaluation
- Peripheral Nerve Disorders
Their work focuses on developing clinical efficacy measures for neurological conditions affecting motor function.
Autoimmune Disorders
Specialized research in autoimmune neurological conditions, particularly Chronic Inflammatory Demyelinating Polyneuropathy (CIDP) and Generalized Myasthenia Gravis. The investigator evaluates novel therapeutic approaches for these conditions.
- Long-term Safety Assessments
- Subcutaneous Treatment Administration
- Autoimmune Response Modification
Their research encompasses both traditional and innovative treatment delivery methods for autoimmune conditions.
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