Philippe R.
- Country
- France
- Department
- Service de Pneumo-Allergologie Pédiatrique
Research Overview
- Study of BI 1015550 and nerandomilast to assess safety, dosing and efficacy in children and adolescents with fibrosing interstitial lung disease
- Evaluation of Long-term Safety and Efficacy of Tezacaftor, Deutivacaftor, and Vanzacaftor Combination Therapy in Patients with Cystic Fibrosis
- Evaluation of Methylprednisolone Efficacy in Neuroendocrine Cell Hyperplasia of Infancy: A Phase I Study
Data & Insights
Has run more than one trial at 63 of 120 partner sites.
Specializations
Pediatric Respiratory and Airway Disease
Clinical activity is centered on pediatric pulmonology, with emphasis on chronic and severe respiratory disorders managed in a hospital setting. The therapeutic scope includes cystic fibrosis, bronchiectasis, asthma, and bronchiectasis-associated infectious complications, alongside broader respiratory tract diseases.
- Cystic fibrosis
- Severe asthma
- Bronchiectasis
- Chronic obstructive pulmonary disease
Research involvement also extends to pulmonary fibrosis, interstitial lung disease, and pulmonary hypertension, reflecting interest in progressive respiratory conditions and complex airway inflammation.
Inflammatory and Autoimmune Disorders
The investigator is active in trials addressing immune-mediated disease across gastroenterology, rheumatology, and dermatology. This includes ulcerative colitis, Crohn's disease, systemic lupus erythematosus, and vasculitis, as well as chronic inflammatory skin conditions.
- Ulcerative colitis
- Crohn's disease
- Systemic lupus erythematosus
- Hidradenitis suppurativa
Additional interest is seen in atopic dermatitis, prurigo nodularis, pemphigus, and Behçet's disease, indicating a strong therapeutic focus on chronic immune dysregulation.
Pediatric Neurology and Rare Genetic Disease
Research involvement includes neurology and rare pediatric disorders affecting development, movement, and seizure control. The clinical landscape covers epilepsy, tuberous sclerosis complex, Rett syndrome, and spinal muscular atrophy.
- Epilepsy
- Tuberous sclerosis complex
- Spinal muscular atrophy
- Rett syndrome
Work also spans developmental and epileptic encephalopathies, cerebral palsy, Parkinson's disease, and selected neurodevelopmental disorders, highlighting engagement with complex neurological care in children and adolescents.
Pediatric Growth, Metabolic, and Genetic Conditions
The investigator has interest in endocrine, metabolic, and genetic disease in younger patients, with trials involving obesity, achondroplasia, hypoparathyroidism, and metachromatic leukodystrophy.
- Obesity
- Achondroplasia
- Hypoparathyroidism
- Metachromatic leukodystrophy
Further areas include Gaucher disease, mucopolysaccharidosis, hyperoxaluria, and cystic fibrosis-related nutrition, showing a broad therapeutic reach in inherited and metabolic disorders.
Hematology, Oncology, and Transplant-Related Care
Clinical trial activity also covers hematology, oncology, and transplant medicine, with involvement in leukemia, lymphoma, multiple myeloma, and solid tumors. The portfolio includes diseases such as acute myeloid leukemia, diffuse large B-cell lymphoma, and non-small cell lung cancer.
- Acute myeloid leukemia
- Diffuse large B-cell lymphoma
- Multiple myeloma
- Non-small cell lung cancer
There is also activity in graft-versus-host disease, hemophilia, and thrombotic and cardiovascular complications, reflecting a broad therapeutic interest in advanced hospital-based innovation.
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