Odile B. T.
- Country
- France
- Department
- Neuro-Pediatric
Research Overview
- ION356-CS1: A Phase 1b Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Patients with Pelizaeus-Merzbacher Disease
- Long-term Safety, Tolerability, and Efficacy Evaluation of Givinostat in Duchenne Muscular Dystrophy Patients Previously Enrolled in Givinostat Trials
Data & Insights
Has run more than one trial at 0 of 29 partner sites.
Specializations
Neuromuscular Disorders
The investigator specializes in the therapeutic management of Duchenne Muscular Dystrophy (DMD), conducting research into innovative treatment approaches for this progressive muscle-wasting condition.
- Long-term therapeutic interventions
- Safety and tolerability assessment
- Muscle function preservation
Active involvement in evaluating novel therapeutic compounds for DMD patients, with particular attention to long-term treatment outcomes.
Rare Neurological Conditions
The investigator focuses on treatment development for Pelizaeus-Merzbacher Disease, a rare genetic disorder affecting the central nervous system.
- Early-phase therapeutic evaluation
- Pharmacological research
- Rare disease interventions
Dedicated to advancing therapeutic options for patients with rare neurological disorders through clinical investigation of novel compounds.
Clinical Development
The investigator engages in safety and efficacy evaluation of experimental therapeutics, with expertise in both initial and extended treatment protocols.
- Drug safety assessment
- Long-term patient monitoring
- Treatment tolerability studies
Specialized in conducting comprehensive clinical evaluations to establish therapeutic safety profiles in neurological conditions.
Related Investigators
Researchers in similar fields or departments
Want to know more about this investigator?
We can share extended profile information and contact details.
Is something out of date?
Tell us what needs correcting and we'll update this profile.