Benedicte N.
- Country
- France
- Department
- Pediatric immunohematology and rheumatology department
Research Overview
- Phase I/II Open‑Label Study Assessing Safety and Efficacy of LV‑FOXP3‑T4 Induced CD4⁺ Treg Cell Therapy ± Low‑Dose Aldesleukin in Patients with IPEX Syndrome
- Evaluation of Leniolisib Phosphate in Pediatric Patients Aged 4-11 with Activated Phosphoinositide 3-Kinase Delta Syndrome: Safety, Pharmacokinetics, and Efficacy
- Phase 3 Multicenter Study of Tabelecleucel in Epstein-Barr Virus-Associated Post-Transplant Lymphoproliferative Disease Post-Rituximab Failure
Data & Insights
Has run more than one trial at 7 of 34 partner sites.
Specializations
Rare Immunological Disorders
Specializes in treating Activated Phosphoinositide 3-Kinase Delta Syndrome (APDS), a rare genetic disorder affecting immune system function. The investigator's work focuses on pediatric applications of novel therapeutic approaches for this condition.
- Pediatric APDS Management
- Genetic Immunodeficiency Treatment
- Targeted Immunological Therapy
Expertise includes evaluating treatment responses in young patients aged 4 to 11 years with immunological disorders.
Post-Transplant Complications
Focuses on treating Epstein-Barr Virus-Associated Post-Transplant Lymphoproliferative Disease (EBV+ PTLD) in transplant recipients. Specializes in managing complications following both solid organ and hematopoietic cell transplantation.
- Transplant-Related Lymphoproliferative Disorders
- EBV-Specific Immunotherapy
- Advanced Cellular Therapy
Particular interest in developing treatment strategies for patients who have failed conventional therapies.
Hematological Complications
Expertise in treating Pure Red Cell Aplasia (PRCA) following allogeneic hematopoietic stem cell transplantation, particularly in cases involving ABO blood type mismatches. Specializes in innovative antibody-based treatments for post-transplant hematological disorders.
- Post-Transplant Anemia Management
- Monoclonal Antibody Therapy
- Blood Type Mismatch Complications
Advanced experience in developing targeted therapeutic approaches for transplant-related hematological conditions.
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