Beatriz V. M.
- Country
- Spain
- Department
- #3104:Onco Hematología
Research Overview
- Phase 1/2 Study of Subcutaneous Blinatumomab in Adults and Adolescents with Relapsed/Refractory or MRD+ B-cell Precursor Acute Lymphoblastic Leukemia
- Safety and Efficacy of Asciminib, Blinatumomab, and Combination Therapy in Pediatric and Young Adult Patients with Relapsed/Refractory BCR::ABL1+ or Ph-like ALL
- Asciminib in Pediatric Philadelphia-Positive Chronic Myeloid Leukemia in Chronic Phase With or Without T315I Mutation: Phase II Safety and Efficacy Study
Data & Insights
Has run more than one trial at 60 of 123 partner sites.
Specializations
Pediatric Oncology & Hematology
Specializes in malignant disorders of the blood and solid organs in children and adolescents, emphasizing high‑risk and relapsed disease.
- Acute Lymphoblastic Leukemia
- Acute Myeloid Leukemia
- Neuroblastoma
- Medulloblastoma
- Langerhans Cell Histiocytosis
Research integrates molecular profiling to guide targeted therapies.
Rare Genetic & Metabolic Disorders
Addresses inherited conditions with hematologic or systemic impact, often requiring gene‑based interventions.
- Fanconi Anemia
- Pyruvate Kinase Deficiency
- Mucopolysaccharidosis Type II
- Niemann‑Pick C Disease
- Inherited Metabolic Disorders
Clinical studies evaluate long‑term safety of enzyme replacement and gene‑therapy approaches.
Immunological & Allergic Diseases
Focuses on immune‑mediated skin and respiratory conditions prevalent in the pediatric population.
- Atopic Dermatitis
- Severe Asthma
- Food Allergy
- Allergic Rhinoconjunctivitis
- Severe Cow's Milk Allergy
Investigations include biologic agents and immunomodulatory therapies.
Transplantation & Graft‑Versus‑Host Disease
Dedicated to outcomes after hematopoietic stem cell transplantation and management of associated complications.
- Acute Graft‑Versus‑Host Disease
- Chronic Graft‑Versus‑Host Disease
- Hematopoietic Stem Cell Transplant
- Immune Reconstitution
- Transplant‑Related Infections
Efforts aim to improve survival and reduce long‑term morbidity.
Neurodevelopmental & Neurological Disorders
Targets epilepsy syndromes and neurogenetic conditions that affect cognition and motor function.
- Dravet Syndrome
- Tuberous Sclerosis Complex
- Rett Syndrome
- Lennox‑Gastaut Syndrome
- Developmental and Epileptic Encephalopathies
Clinical programs explore novel antiepileptic agents and precision medicine strategies.
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